Trial NCT02030015

View at ClinicalTrials.gov 
Org. Study IDs: Syner_G_Regimen
Secondary IDs: 1311M46101 U54NS065768

Last trial update was posted on 2021-04-14

MeSH Interventions

Miglustat

MeSH Conditions

Gangliosidoses Gangliosidoses, GM2 Gangliosidosis, GM1 Sandhoff Disease Tay-Sachs Disease

Other Conditions

GM1 Gangliosidoses GM2 Gangliosidoses

Stopping Reasons

Efficacy

Limitations And Caveats

N/A

Result Publications


Annotations

Category Annotations
No annotators decided on categories yet

Intervention Annotations
# Outdated Intervention Condition
Name Route DrugBank ID