Trial NCT00688597

View at ClinicalTrials.gov 
Org. Study IDs: POM-CL-201

Last trial update was posted on 2018-08-17

MeSH Interventions

1-Deoxynojirimycin

MeSH Conditions

Glycogen Storage Disease Type II

Other Conditions

Pompe Disease

Stopping Reasons

Per protocol, 3 sequential dose cohorts were planned. Study discontinued by Sponsor based upon serious adverse events in first 2 of 3 participants in Cohort 1.

Limitations And Caveats

The serious adverse event of muscle weakness was the main contributor to the study not reaching the target number of participants needed to achieve target power and statistically reliable results.

Result Publications

N/A

Annotations

Category Annotations
No annotators decided on categories yet

Intervention Annotations
# Outdated Intervention Condition
Name Route DrugBank ID